RARE DISEASE TRIALS
Rare Disease Research Requires a Precision Approach from a Precision CRO
Rare diseases collectively affect about 300 million people globally. With support from regulatory agencies, pharmaceutical and biotech companies have narrowed their focus to target these specialized populations.
What makes rare disease research so valuable also makes it frustrating. Clinical trials in this area struggle due lack of patient recruitment, lack of disease understanding and lack of funding.
If your company is researching a treatment or cure for one of the close to 6,000 current rare diseases, partner with a CRO that knows how to overcome its many clinical, logistical, and regulatory challenges.
Biorasi has supported sponsors in the following rare disease trials:
- Dermatological Rare Diseases
- Generalized Pustular Psoriasis (GPP)
- Palmoplantar Pustulosis (PPP)
- Xeroderma Pigmentosum (XP)
- Dermatological Rare Diseases
- Genetic Rare Diseases
- Mucopolysaccharidosis Type II (MPS II)
- Genetic Rare Diseases
- Hematological Rare Diseases
- Hereditary Hemorrhagic Telangiectasia (HHT)
- Paroxysmal Nocturnal Hemoglobinuria (PNH)
- Thalassemia
- Hematological Rare Diseases
- Infectious Rare Diseases
- Hepatitis D Virus
- Infectious Rare Diseases
- Nephrological Rare Diseases
- Calciphylaxis/calcific uremic arteriolopathy (CUA)
- Complement 3 Glomerulopathy (C3G)
- Focal Segmental Glomerulosclerosis (FSGS)
- Immunoglobulin A (IgA) Nephropathy
- Lupus Nephritis (LN)
- Nephrological Rare Diseases
- Neurological Rare Diseases
- Amyotrophic Lateral sclerosis (ALS)
- Friedreich’s Ataxia (FRDA)
- Multiple Sclerosis (MS)
- Neurological Rare Diseases
- Oncological Rare Diseases
- Biliary Tract Cancer
- Glioblastoma (GBM)
- Multiple Myeloma (MM)
- Renal Cell Carcinoma (RCC)
- Oncological Rare Diseases
- Ophthalmological Rare Diseases
- Non-Infectious Uveitis (NIU)
- Pediatric Cataracts
- Ophthalmological Rare Diseases
- Pulmonological (Respiratory) Rare Diseases
- Autoimmune Pulmonary Alveolar Proteinosis (aPAP)
- Non-Tuberculosis Mycobacterium Infection (NTM)
- Cystic Fibrosis (CF)
- Idiopathic Pulmonary Fibrosis (IPF)
- Pulmonological (Respiratory) Rare Diseases
RARE DISEASE DAY
In observance of Rare Disease Day 2020, Biorasi, LLC held a company-wide event and fundraiser to raise awareness for Angelman Syndrome. The event took place on Friday, February 2020, and 78 employees contributed over $4,000 to the Foundation for Angelman Syndrome Therapeutics (FAST)
We Optimize Patient Recruitment for Rare Disease Research
Do you worry whether you’ll find enough patients for your clinical trial? Whether you need to add sites internationally, recruit using patient registries, conduct a virtual or hybrid trial, or a combination of these methods, the Biorasi team knows how to recruit the patients you need for a successful study.
Review our checklist
We prepared a Rare Disease Checklist to help you understand the challenges and opportunities running these unique trials.
Connect with us to find the right strategy for your next RARE DISEASE trial. CONTACT US TODAY
Connect with us to find the right strategy for your next dermatology trial. CONTACT US TODAY
